News for Healthier Living

Single-Dose Gene Therapy is Potentially Life-Changing for Adults with Hemophilia B

Adults with hemophilia B saw their number of bleeding episodes drop by an average of 71 percent after a single infusion of gene therapy, according to the results of an international Phase III clinical trial published today in the New England Journal of Medicine by researchers from the University of Pennsylvania Perelman School of Medicine and a multicenter group of investigators.

September 25, 2024


October 5 2024

October 4 2024

October 3 2024

October 2 2024

October 1 2024

September 30 2024

September 29 2024

September 28 2024

September 27 2024

September 26 2024

September 25 2024

September 24 2024

September 23 2024

September 22 2024

September 21 2024